February 21, 2025

FDA Approves First Cerebrotendinous Xanthomatosis Treatment

The FDA has approved Ctexli (chenodiol) as the first treatment for cerebrotendinous xanthomatosis, a rare lipid storage disorder.

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February 20, 2025

18-Year Neuroblastoma Remission in a Patient After GD2 CAR T-Cell Therapy

"She has never required any other therapy and is likely the longest-surviving patient with cancer who received [CAR T-cell] therapy."

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February 20, 2025

Hospital Occupancy to Reach 85% by 2035

The projection is driven by a decline in staffed beds and an aging population.

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February 19, 2025

Hospital Occupancy to Reach 85% by 2035

The projection is driven by a decline in staffed beds and an aging population.

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February 19, 2025

CRISPR Successfully Removes Extra Chromosome 21

Researchers demonstrate first successful targeted removal of extra chromosome 21 in Down syndrome cells using CRISPR-Cas9, achieving up to 30.6% effectiveness in laboratory studies.

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February 18, 2025

AAP Guide Targets Early Biliary Atresia

New AAP clinical report outlines a three-step screening strategy for primary care providers to identify biliary atresia in infants by 2-4 weeks of life, potentially reducing the need for liver transplants.

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February 14, 2025

New Blood-Clotting Disorder Linked to Antibodies

Scientists have identified a chronic blood-clotting condition characterized by treatment-resistant thrombosis and linked to monoclonal antibodies targeting platelet factor 4, according to a new study.

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February 14, 2025

Study: Patients Trust Female Docs Less

Study findings and an interview with the lead investigator.

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February 12, 2025

FDA & EMA: Submitted Trial Data Discrepancies

Sample size discrepancies were identified in 13 trials (65%), with 8 differing by more than 10%.

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