November 25, 2025

FDA OKs First SMA Gene Replacement Therapy

The FDA approved Itvisma, the first gene replacement therapy for children 2 years and older, teens, and adults with spinal muscular atrophy, a one-time treatment that replaces the SMN1 gene and demonstrated improved motor function in Phase 3 studies.

Conexiant

November 21, 2025

EULAR: Issues With the RA Definition?

Researchers examine the strengths and shortcomings of the current European Alliance of Associations for Rheumatology definition for difficult-to-treat rheumatoid arthritis.

Conexiant

November 20, 2025

Severe Infection: Are Hidden Immune Signals Emerging?

Researchers identify four reproducible immune endotypes across sepsis and critical illness.

Conexiant

November 19, 2025

What the Storms Left Behind Was Worse

Severe storm-related mold infestations are contributing to ongoing respiratory and systemic health risks amid significant delays in remediation and disaster recovery support.

KFF Health News

November 17, 2025

‘Patent Dance’ Delays Biosimilars Despite FDA Shift

The FDA moves to speed biosimilar approvals, but rising patent barriers may still delay lower-cost alternatives.

Conexiant

November 13, 2025

‘FDA Said Yes, Despite Inconclusive Evidence’

The FDA’s authorization of the Q-Collar is under scrutiny after researchers identified duplicated data, altered study endpoints, and unsubstantiated “brain protection” claims.

Conexiant

November 10, 2025

Can Mucoactive Therapy Change Bronchiectasis Outcomes?

Researchers examine mucoactive therapy effectiveness in bronchiectasis management.

Conexiant

November 05, 2025

Shame in Medicine—A Quiet Epidemic

A new movement in medicine aims to teach “shame competence,” helping physicians recognize and manage one of the field’s most corrosive yet overlooked emotions.

KFF Health News

November 04, 2025

FDA Approves First Drug for Thymidine Kinase 2 Deficiency

First-ever treatment shows significant survival benefit in matched-pair analysis of this ultra-rare mitochondrial depletion syndrome.

Conexiant